Although uncommon in the general population, over 7000 rare diseases affect more than 30 million Americans and 350 million people globally. Rare diseases present many unique challenges for patients and physicians, from diagnosis to treatment and for biopharma companies, from discovery to commercialization.
Please join us for this HBA New England region Women in Science event to learn about unique challenges and opportunities in rare diseases. The program will feature success stories of transformative therapies, highlighting scientific breakthroughs and innovative commercialization strategies, that have ultimately delivered life-changing medicines to this small but mighty population.
Healthcare industry professionals at all levels who are interested in learning about rare diseases and transformative medicines are invited to attend this presentation, panel discussion and networking event.
5:30 - 6:15 PM Registration and networking
6:15 - 6:30 PM Welcome and opening remarks
6:30 - 7:30 PM Success stories presentations
7:30 - 8:00 PM Panel discussion and Q&A
8:00 - 8:30 PM Networking
Alnylam is a five-minute walk from the Kendall/MIT MBTA station. Public parking is available on the street or at the Kendall Square South Garage at 350 Kendall St. Please click here to view a site map.
Event is open to: HBA members and nonmembers
Online registration deadline: 13 June 2019
Onsite (walk-in) registration: Is allowed
Onsite registration is not recommended. If you choose to register onsite, please arrive at least fifteen minutes
early and be prepared to use your smartphone/mobile device to complete the transaction. Only credit card
payments are accepted. Nonmembers are advised to create an HBA profile prior to arriving.
Is this event refundable? Yes
If yes, requests must be submitted in writing to firstname.lastname@example.org by 11 June 2019; no refunds are available after this date.
1. Understand the unique challenges and opportunities with rare diseases.
2. Learn how leading biopharma organizations are taking innovative approaches to deliver transformative medicines to rare disease patients.